Gene therapy – for so long something that belonged to the future – has just hit the streets.
- Elizabeth Finkel
- The Conversation
A couple of weeks back, you might have picked up a headline alerting us to the most expensive drug in history – a one off gene therapy cure for spinal muscular atrophy.
Novartis have priced the drug Zolgensma at A$3 million (US$2.1 million).
Traditionally a parent of a baby with spinal muscular atrophy was told: take your baby home and love her or him.
Have no false hope, the baby will die paralysed and unable to eat or talk by the…
What’s the narrative…